Gene therapy is an advanced medical technique that involves modifying a person's genes to treat or cure a disease. It typically involves introducing a functional gene into a patient's cells to replace a missing or defective one, or modifying existing genes to fight disease. Gene Therapy Products (GTPs) are the vectors or cells used in this process, carrying the therapeutic genetic material.
ICMR published “National Guidelines for Gene Therapy Product Development and Clinical Trials”. Which of the following statements are correct about Gene Therapy Product (GTP) ? 1. It is defined as any biological entity, having the required gene, that could introduce modifications in the genome for therapeutic benefit. 2. GTPs work by repairing, replacing or deactivating disease-causing genes to restore normal function. 3. As per the New Drugs and Clinical Trial Rules (2019), the GTPs falls under ‘new drug’ and shall always be deemed as ‘new drug’. 4. Thalassemia, Gaucher's disease, Sickle cell anaemia and Haemophilia fall under the genetically inherited disease category. Select the correct answer using the code given below :
Asked in PPSC CS Prelims 2021 · Topic: Genetic Engineering and Biotechnology (Applications in Healthcare: Gene Therapy, Recombinant Vaccines, Molecular Diagnostics)
More Biology questions
- Match the below products of biotechnology with their application for treatment of various diseases/disorders. A B 1. Treating Haemophil‐
- The hybridoma technique was developed by whom ?
- Sinovac given for Covid-19 is a
- With reference to recent developments regarding Recombinant Vector Vaccines, consider the following statements: Genetic engineering is applied in the development of these vaccines. Bacteria and viruses are used as vectors. Which of the statements given above is/are correct?
- The 2024 Nobel Prize in Physiology or Medicine was awarded to Victor Ambros and Gary Ruvkun for discovering :
- Rajiv Gandhi Centre for Biotechnology is situated at
- In the context of the developments in Bioinformatics, the term 'transcriptome', sometimes seen in the news, refers to
- ‘Aerial metagenomics’ best refers to which one of the following situations?